We offer you the safety of our experience

 

Our experience


Rare diseases


Regarding the area of rare diseases, their diagnostics and treatment, we have accumulated broad experience with projects on many levels. We have collaborated with patient organisations, payers, regulators and pharmaceutical manufacturers.

 

Our experience includes for example the following areas

  • -  Cystic fibrosis
  • -  Phenylketonuria
  • -  Gaucher's disease
  • -  Primary biliary cirrhosis
  • -  Spinal muscular atrophy
  • -  West syndrome
  • -  Fabry disease
  • -  Hepatic porphyria
  • -  Nephropathic cystinosis
  • -  Paediatric haemangioma

Our most recent projects include

  • -  National cost-of-illness studies
  • -  Cost-of-illness surveys from patient perspective
  • -  Preparation of submission of reimbursement dossier for CZ / SK
  • -  Argumentation plan and documentation for negotiations with payers
  • -  Interactive budget impact model
  • -  De novo developed pharmacoeconomic model